RESEARCHER RESOURCES
CLINICAL TRIALS & OBSERVATIONAL STUDIES
Here are links and resources for the latest clinical trials.
Interventional (Clinical Trial)
A Phase 2 Safety, Tolerability, and Proof-of-Concept Study of VGL101 in Patients With Adult-Onset Leukoencephalopathy With Axonal Spheroids and Pigmented Glia (ALSP).
For more details on the Vigil Neuroscience VGL101 clinical trial visit the Ignite website:
Illuminate Natural History Study
The main purpose of the study is to learn more about how ALSP occurs and how the disease affects patients over time. Study participants will not receive any investigational drugs as part of this study and will continue their standard of care treatment during the study.
BONE MARROW TRANSPLANT
Masonic Cancer Center, University of Minnesota – Minneapolis, Minnesota
Mayo Clinic – Jacksonville, Florida
The Myelin Disorders Biorepository Project
The Myelin Disorders Biorepository Project (MDBP) seeks to collect and analyze clinical data and biological samples from leukodystrophy patients worldwide to support ongoing and future research projects.
Modeling Macrophages Activation Pattern...
This study is a national, non-randomized, open-label, multi-site with minimal risk study in adult with adrenomyeloneuropathy (AMN), childhood and adult subjects with cerebral ALD (cALD), juvenile/adult metachromatic leukodystrophy (MLD) and adults with leukoencephalopathy and axonal spheroids and pigmented glia (ALSP). 49 subjects will be enrolled with one blood sample collection during one of their medical follow-up visit.
Clinical Research on Adult-Onset Leukoencephalopathy With ALSP
Dr. La Piana, MD, PhD, Professor in McGill’s Department of Neurology and Neurosurgery, explains her research in axonal spheroids and pigmented glia.
Search Keywords On clinicaltrails.gov
- ALSP
- HDLS
- Hereditary Leukoencephalopathy with Axonal Spheroids
- CSF1R
- CSF1R Related Leukoencephalopathy
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